Did you know Panasonic made the first mirrorless camera back in 2008? This History of Lumix countdown breaks down 13 world-first cameras ...

Adeno-associated virus serotype 9 gene therapy increased beta-galactosidase in nine type II GM1 gangliosidosis patients. Most adverse events were moderate and transient; one serious event was directly ...

Rare disease families need to stand up and be counted if they want things to change said mum and advocate Christine Waggoner. She spoke to pharmaphorum as part of our Patients Insights series. Like ...