An oral pyruvate kinase (PK) activator, mitapivat becomes the only approved option for treating anemia in both ...

Here is the full list of the health and wellness Startup Battlefield 200 selectees, along with a note on what made us select ...

Approval was based on the phase 3 ENERGIZE and ENERGIZE-T studies evaluating the safety and efficacy of mitapivat in adults with alpha- or beta-thalassemia.

Major is one of the first pediatric patients in Florida to receive gene therapy for sickle cell disease since the FDA ...

There can be too much of a good thing as some seemingly “good for you” foods could be secretly sabotaging your health if you ...

Agios Pharmaceuticals has announced a major regulatory milestone with the U.S. Food and Drug Administration approving ...

OHSU lab started exploring new use of the drug 30 years ago; now, it may improve techniques to measure, monitor aggressive ...

The FDA has expanded the indication of ferric maltol (Accrufer) capsules to include adolescents aged 10 years and older, ...

Dr. Nassir Marrouche is director of the Heart and Vascular Institute at Tulane University with a subspecialty in ...

A clinical trial at the National Institutes of Health (NIH) has shown that an experimental treatment for patients with severe aplastic anemia resulted ...

AQVESME is the only FDA-approved medicine for anemia in both non-transfusion-dependent and transfusion-dependent alpha- or beta-thalassemia Marketed under AQVESME brand name in the U.S. for ...